BCHO Grand Rounds: Gene Therapies in Mucopolysaccharidoses

Presented by:
Paul Harmatz, MD
Pediatric Gastroenterology and Nutrition
UCSF Benioff Children's Hospital Oakland

Objectives:

• Identify/diagnose the major types of mucopolysaccharidoses (MPS).
• List present therapies for MPS disease and identify the unmet medical needs.
• Assess the progress in gene therapy for MPS disease.
• Recognize the progress and importance of newborn screening in early diagnosis of MPS.

CME/CEU
UCSF Benioff Children’s Hospital Oakland is accredited by the Institute for Medical Quality/California Medical Association (IMQ/CMA) to provide continuing medical education for physicians.
UCSF Benioff Children’s Hospital Oakland designates this live activity for a maximum of 1 AMA PRA Category 1 Credit™.

Physicians should claim only the credit commensurate with the extent of their participation in the activity. 

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